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Advancing Novel Treatments for Patients with Muscle Disease

Kate Therapeutics regularly attends industry and scientific events and publishes its research and findings in peer-reviewed journals.

Events / Presentations

American Society of Gene & Cell Therapy (ASGCT) 2024

Oral Presentation
Directed evolution of novel MyoAAV capsid variants enabling effective systemic muscle transduction while de-targeting the liver in non-human primates

Oral Presentation
Developing Highly Potent and Safe Muscle Gene Therapy Candidates by Combining Effective Liver De-targeted MyoAAV Capsids and Cell Type Specific Regulatory Elements

Poster Presentation
Developing a potent gene therapy candidate for facioscapulohumeral muscular dystrophy (FSHD) through high throughput AAV capsid and cargo engineering [495]

Poster Presentation
Highly effective expression of full-length Dysferlin protein in Bla/J mouse muscle after systemic MyoAAV administration [1489]

We are Focused on Delivering Life-Changing Therapies to Patients

We are applying technology platforms that address the key limitations of current gene therapies, including tissue-specific delivery and gene regulation.